Craig M. McDonald | Scholar Profiles and Rankings

Publications and Citation History

Publications based on Top Specialties

Types of Publication

Publications
Books
Patents
NIH/NSF

Add Delete
Survival among patients receiving eteplirsen for up to 8 years for the treatment of Duchenne muscular dystrophy and contextualization with natural history controls (journal article) Iff, Joel \| Done, Nicolae \| Tuttle, Edward \| Zhong, Yi \| Wei, Fangzhou \| Darras, Basil T. \| McDonald, Craig M. \| Mercuri, Eugenio \| Muntoni, Francesco Muscle & Nerve, volume 70, issue 1, pages 60-70 (2024). 10.1002/mus.28075 Cited by (2) \| Cite \| Source
Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials (journal article) McDonald, Craig M. \| Signorovitch, James \| Mercuri, Eugenio \| Niks, Erik H. \| Wong, Brenda \| Fillbrunn, Mirko \| Sajeev, Gautam \| Yim, Erica \| Dieye, Ibrahima \| Miller, Debra \| ... \| Goemans, Nathalie PLOS ONE, volume 19, issue 6, pages e0304099- (2024). 10.1371/journal.pone.0304099 Cite \| Source
Practical Considerations for Delandistrogene Moxeparvovec Gene Therapy in Patients With Duchenne Muscular Dystrophy (journal article) Mendell, Jerry R. \| Proud, Crystal \| Zaidman, Craig M. \| Mason, Stefanie \| Darton, Eddie \| Wang, Shufang \| Wandel, Christoph \| Murphy, Alexander P. \| Mercuri, Eugenio \| Muntoni, Francesco \| McDonald, Craig M. Pediatric Neurology, volume 153 (2024). 10.1016/j.pediatrneurol.2024.01.003 Cited by (5) \| Cite \| Source
Draft Guidance for Industry Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and Related Dystrophinopathies – Developing Potential Treatments for the Entire Spectrum of Disease (journal article) McDonald, Craig \| Camino, Eric \| Escandon, Rafael \| Finkel, Richard S. \| Fischer, Ryan \| Flanigan, Kevin \| Furlong, Pat \| Juhasz, Rose \| Martin, Ann S. \| Villa, Chet \| Sweeney, H. Lee Journal of Neuromuscular Diseases, volume 11, issue 2, pages 499-523 (2024). 10.3233/JND-230219 Cite \| Source
Gait Event Detection and Travel Distance Using Waist-Worn Accelerometers across a Range of Speeds: Automated Approach (journal article) Ramli, Albara Ah \| Liu, Xin \| Berndt, Kelly \| Chuah, Chen-Nee \| Goude, Erica \| Kaethler, Lynea B. \| Lopez, Amanda \| Nicorici, Alina \| Owens, Corey \| Rodriguez, David \| ... \| Henricson, Erik K. Sensors, volume 24, issue 4, pages 1155- (2024). 10.3390/s24041155 Cite \| Source
Gait Characterization in Duchenne Muscular Dystrophy (DMD) Using a Single-Sensor Accelerometer: Classical Machine Learning and Deep Learning Approaches (journal article) Ramli, Albara Ah \| Liu, Xin \| Berndt, Kelly \| Goude, Erica \| Hou, Jiahui \| Kaethler, Lynea B. \| Liu, Rex \| Lopez, Amanda \| Nicorici, Alina \| Owens, Corey \| ... \| Henricson, Erik K. Sensors, volume 24, issue 4, pages 1123- (2024). 10.3390/s24041123 Cited by (1) \| Cite \| Source
Assessing the value of delandistrogene moxeparvovec (SRP-9001) gene therapy in patients with Duchenne muscular dystrophy in the United States (journal article) Klimchak, Alexa C. \| Sedita, Lauren E. \| Rodino-Klapac, Louise R. \| Mendell, Jerry R. \| McDonald, Craig M. \| Gooch, Katherine L. \| Malone, Daniel C. Journal of Market Access & Health Policy, volume 11, issue 1 (2023). 10.1080/20016689.2023.2216518 Cited by (2) \| Cite \| Source
Delandistrogene Moxeparvovec Gene Therapy in Ambulatory Patients (Aged ≥4 to <8 Years) with Duchenne Muscular Dystrophy: 1‐Year Interim Results from Study SRP ‐9001‐103 ( ENDEAVOR ) (journal article) Zaidman, Craig M. \| Proud, Crystal M. \| McDonald, Craig M. \| Lehman, Kelly J. \| Goedeker, Natalie L. \| Mason, Stefanie \| Murphy, Alexander P. \| Guridi, Maitea \| Wang, Shufang \| Reid, Carol \| ... \| Mendell, Jerry R. Annals of Neurology, volume 94, issue 5, pages 955-968 (2023). 10.1002/ana.26755 Cited by (16) \| Cite \| Source
Sleep Disordered Breathing in Children with Neuromuscular Disease (journal article) Chidambaram, Ambika G. \| Jhawar, Sanjay \| McDonald, Craig M. \| Nandalike, Kiran Children, volume 10, issue 10, pages 1675- (2023). 10.3390/children10101675 Cited by (2) \| Cite \| Source
Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015–2022): 2022 interim analysis (journal article) Mercuri, Eugenio \| Osorio, Andrés Nascimento \| Muntoni, Francesco \| Buccella, Filippo \| Desguerre, Isabelle \| Kirschner, Janbernd \| Tulinius, Már \| de Resende, Maria Bernadete Dutra \| Morgenroth, Lauren P. \| Gordish-Dressman, Heather \| ... \| McDonald, Craig M. Journal of Neurology, volume 270, issue 8, pages 3896-3913 (2023). 10.1007/s00415-023-11687-1 Cited by (9) \| Cite \| Source
Efficacy and Safety of Viltolarsen in Boys With Duchenne Muscular Dystrophy: Results From the Phase 2, Open-Label, 4-Year Extension Study (journal article) Clemens, Paula R. \| Rao, Vamshi K. \| Connolly, Anne M. \| Harper, Amy D. \| Mah, Jean K. \| McDonald, Craig M. \| Smith, Edward C. \| Zaidman, Craig M. \| Nakagawa, Tomoyuki \| Hoffman, Eric P. Journal of Neuromuscular Diseases, volume 10, issue 3, pages 439-447 (2023). 10.3233/JND-221656 Cited by (14) \| Cite \| Source
Modeling Early Heterogeneous Rates of Progression in Boys with Duchenne Muscular Dystrophy (journal article) Fang, Yuan \| McDonald, Craig M. \| Clemens, Paula R. \| Gordish, Heather-Dressman \| Illei, Kate \| Hoffman, Eric P. \| Dang, Utkarsh J. Journal of Neuromuscular Diseases, volume 10, issue 3, pages 349-364 (2023). 10.3233/JND-221527 Cited by (3) \| Cite \| Source
Microdystrophin Expression as a Surrogate Endpoint for Duchenne Muscular Dystrophy Clinical Trials (journal article) Chamberlain, Jeffrey S. \| Robb, Melissa \| Braun, Serge \| Brown, Kristy J. \| Danos, Olivier \| Ganot, Annie \| Gonzalez-Alegre, Pedro \| Hunter, Nina \| McDonald, Craig \| Morris, Carl \| ... \| Duan, Dongsheng Human Gene Therapy, volume 34, issue 9-10, pages 404-415 (2023). 10.1089/hum.2022.190 Cited by (5) \| Cite \| Source
Ataluren Preserves Upper Limb Function in nmDMD Patients from Study 041, a Phase 3 Placebo-Controlled Trial, and the STRIDE Registry (S34.008) (journal article) McDonald, Craig M. \| Mercuri, Eugenio \| Muntoni, Francesco \| Gordish-Dressman, Heather \| Morgenroth, Lauren P. \| de Resende, Maria Bernadete Dutra \| Zhou, Shuizhen \| Neeharika, Mathukumalli Lakshmi \| Haginoya, Kazuhiro \| Ramos-Platt, Leigh \| ... \| Trifillis, Panayiota Neurology, volume 100, issue 17_supplement_2 (2023). 10.1212/WNL.0000000000202507 Cite \| Source
Disease progression rates in ambulatory Duchenne muscular dystrophy by steroid type, patient age and functional status (journal article) McDonald, Craig M \| Marden, Jessica R \| Shieh, Perry B \| Wong, Brenda L \| Lane, Henry \| Zhang, Adina \| Nguyen, Ha \| Frean, Molly \| Trifillis, Panayiota \| Koladicz, Karyn \| Signorovitch, James Journal of Comparative Effectiveness Research (2023). 10.57264/cer-2022-0190 Cited by (2) \| Cite \| Source
Kinematic changes in gait in boys with Duchenne Muscular Dystrophy: Utility of the Gait Deviation Index, the Gait Profile Score and the Gait Variable Scores (journal article) Sienko, Susan \| Buckon, Cathleen \| Bagley, Anita \| Fowler, Eileen \| Heberer, Kent \| Staudt, Loretta \| Sison-Williamson, Mitell \| McDonald, Craig \| Sussman, Michael Gait & Posture, volume 100 (2023). 10.1016/j.gaitpost.2022.12.007 Cited by (4) \| Cite \| Source
Functional and Clinical Outcomes Associated with Steroid Treatment among Non-ambulatory Patients with Duchenne Muscular Dystrophy1 (journal article) McDonald, Craig M. \| Mayer, Oscar H. \| Hor, Kan N. \| Miller, Debra \| Goemans, Nathalie \| Henricson, Erik K. \| Marden, Jessica R. \| Freimark, Jonathan \| Lane, Henry \| Zhang, Adina \| ... \| Signorovitch, James Journal of Neuromuscular Diseases, volume 10, issue 1, pages 67-79 (2023). 10.3233/JND-221575 Cited by (3) \| Cite \| Source
Longitudinal changes in cardiac function in Duchenne muscular dystrophy population as measured by magnetic resonance imaging (journal article) Batra, Abhinandan \| Barnard, Alison M. \| Lott, Donovan J. \| Willcocks, Rebecca J. \| Forbes, Sean C. \| Chakraborty, Saptarshi \| Daniels, Michael J. \| Arbogast, Jannik \| Triplett, William \| Henricson, Erik K. \| ... \| Walter, Glenn A. BMC Cardiovascular Disorders, volume 22, issue 1 (2022). 10.1186/s12872-022-02688-5 Cited by (6) \| Cite \| Source
Delays in pulmonary decline in eteplirsen‐treated patients with Duchenne muscular dystrophy (journal article) Iff, Joel \| Gerrits, Charles \| Zhong, Yi \| Tuttle, Edward \| Birk, Erica \| Zheng, Yeya \| Paul, Xander \| Henricson, Erik K. \| McDonald, Craig M. Muscle & Nerve, volume 66, issue 3, pages 262-269 (2022). 10.1002/mus.27662 Cited by (12) \| Cite \| Source
Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD): Observations from a phase 2 trial (journal article) Muntoni, Francesco \| Guglieri, Michela \| Mah, Jean K. \| Wagner, Kathryn R. \| Brandsema, John F. \| Butterfield, Russell J. \| McDonald, Craig M. \| Mayhew, Anna G. \| Palmer, Jeffrey P. \| Marraffino, Shannon \| ... \| Mercuri, Eugenio PLOS ONE, volume 17, issue 8, pages e0272858- (2022). 10.1371/journal.pone.0272858 Cited by (5) \| Cite \| Source

Title	Investigators	Year	Cost	Agency
Clinically Meaningful Outcomes for Duchenne Muscular Dystrophy Therapeutic Trials	Mcdonald, Craig M.	2014	$345,978	NATIONAL INSTITUTE OF ARTHRITIS AND MUSCULOSKELETAL AND SKIN DISEASES
Clinically Meaningful Outcomes for Duchenne Muscular Dystrophy Therapeutic Trials	Mcdonald, Craig M.	2013	$306,238	NATIONAL INSTITUTE OF ARTHRITIS AND MUSCULOSKELETAL AND SKIN DISEASES
Clinically Meaningful Outcomes for Duchenne Muscular Dystrophy Therapeutic Trials	Mcdonald, Craig M.	2012	$315,088	NATIONAL INSTITUTE OF ARTHRITIS AND MUSCULOSKELETAL AND SKIN DISEASES
Clinically Meaningful Outcomes for Duchenne Muscular Dystrophy Therapeutic Trials	Mcdonald, Craig M	2011	$327,639	NATIONAL INSTITUTE OF ARTHRITIS AND MUSCULOSKELETAL AND SKIN DISEASES